Genetic Modification Therapies Clinical Applications: Gene Therapies, Genetically Modified Cell...

Genetic Modification Therapies Clinical Applications: Gene Therapies, Genetically Modified Cell Therapies, RNA Therapies and Gene Editing

Report Code: BIO159A

Publish Date: Sep 2018

Publisher: BCC Publishing

Category: Cell Biology

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Report Highlights

The global market for genetic modification therapies should grow from $2.3 billion in 2018 to reach $17.4 billion by 2023, growing at a compound annual growth rate (CAGR) of 49.9% during the forecast period of 2018-2023.

Report Includes

  • 30 data tables and 56 additional tables
  • An overview of the global market for genetic modification therapies
  • Analyses of global market trends with data from 2017, estimates for 2018, and projections of compound annual growth rates (CAGRs) through 2023
  • Information on the genetic variation analysis and genetic modification technologies
  • Evaluation of key growth driving forces, acquisitions and strategic alliances related to the market
  • Detailed description of the criteria for selecting gene modification therapy applications
  • Review of patents for gene editing, gene therapy, RNA therapy and gene modification therapies
  • Profiles of the key companies in the market, including 4d Molecular Therapeutics LLC, Abeona Therapeutics LLC, Acer Therapeutics Inc., Allergan Plc and American Gene Technologies International Inc.

Report Scope

The study scope includes clinical therapies using gene editing, gene therapy, genetically modified cell therapy (chimeric antigen receptor T-cells, or CAR T-cells) or RNA therapy platforms. Delivery technologies covered include AAV, adenovirus, lentivirus, retrovirus, other viral and nonviral. Disease areas covered include cardiology, oncology, ophthalmology, hematology, musculoskeletal, neurology, rare diseases and others. Therapies that are already commercialized or are forecast to be commercialized with the next five years are included.

We analyze key genetic modification therapy technologies and products to determine present and future market status and forecasted growth from 2018 through 2023. We also discuss strategic alliances, industry structures, competitive dynamics, patents and market driving forces.

BCC Research examines the genetic modification therapies industry by market segment, including the following segments: gene editing, gene therapy, CAR T-cell therapy, RNA therapy and lentiviral production. The geographic market for genetic modification therapy products by platform technology is analyzed. Regions include North America, Europe, Asia-Pacific and the rest of the world.

The role of key strategic alliances and acquisitions from Jan. 2016 through June 2018 is discussed.

The challenges involved with pricing for genetic modification therapies that can offer one-time cures for diseases is discussed. Emerging markets for clinical gene editing are analyzed. More than 145 companies in the genetic modification therapies industry are profiled.

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Analyst Credentials

John Bergin has produced successful and highly regarded market research reports in the life science industry for BCC research for more than 10 years. Mr. Bergin has held business development and international sales and marketing positions with Corning Inc., an advanced materials company. He has also held executive management positions with IBC Advanced Technologies, a molecular recognition company specializing in separations. Mr. Bergin's extensive expertise in commercializing new technologies is reflected in his market research reports.

Mr. Bergin received a BS degree in Chemistry and Masters of Business Administration (MBA) degree from Brigham Young University and an MS degree in biotechnology from Johns Hopkins University. John Bergin is a pseudonym of the author.

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Table of Contents

All reports provided in PDF format. For shared licensing options (5+ Users), please call a representative at (+1) 781-489-7301 or contact us at info@bccresearch.com
Title/Chapter NamePagesMember Price
Full Report: Genetic Modification Therapies Clinical Applications: Gene Therapies, Genetically Modified Cell Therapies, RNA Therapies and Gene Editing211Free
Chapter- 1: Introduction9Free
Chapter- 2: Summary and Highlights3Free
Chapter- 3: Overview7Free
Chapter- 4: Technology22Free
Chapter- 5: Genetic Modification Therapy Applications4Free
Chapter- 6: Genetic Modification Therapies Industry11Free
Chapter- 7: Acquisitions and Strategic Alliances10Free
Chapter- 8: Markets for Genetic Modification Therapies61Free
Chapter- 9: Patents9Free
Chapter- 10: Company Profiles75Free

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This is an Excel-only version of the report.

Report Includes

    Total Number of Tables in this Report: 86

  • Summary Table: Global Market for Genetic Modification Therapies, by Disease Category, Through 2023
  • Table 1: Scope of Report
  • Table 2: Genetic Modification Therapies Covered in Report
  • Table 3: Genetic Modification Platforms
  • Table 4: Key Market Growth Driving Forces of Genetic Modification Therapies
  • Table 5: Global Market for Genetic Modification Therapies, by Delivery Technology, Through 2023
  • Table 6: Genetic Modification Therapy Technology Life-Cycle Stage
  • Table 7: Characteristics of the Genetic Modification Therapies Industry
  • Table 8: Chemical Building Blocks of DNA and RNA
  • Table 9: DNA Translation and Transcription
  • Table 10: Long-range DNA Structure
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Genetic Modification Therapies Clinical Applications: Gene Therapies, Genetically Modified Cell Therapies, RNA Therapies and Gene Editing
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